CRISPR gene-editing therapies need more diverse DNA to realize their full potential
Medicine has entered a new era in which scientists have the tools to change human genetics directly, creating the potential...
Genetics and Gene Therapy Research
Genetic Discovery Reveals Who Can Benefit from Preterm Birth Therapy
A UC San Francisco-led study has for the first time identified genetic variants that predict whether a patient is likely...
Australians at the cutting-edge of gene therapy research
From the beginning of the genetic revolution when the double helix DNA model was first described in the 1950s, to...
Human Brain Development Sequencing Reveals New Gene Transcripts
Kateryna Kon//Science Photo Library/CanvaUCLA and University of Pennsylvania researchers have uncovered over 200,000 new gene transcripts in the developing human...
Engineered Virus Crosses Blood-Brain Barrier to Deliver Gene Therapy
Summary: Researchers have engineered a gene therapy delivery vehicle that efficiently crosses the blood-brain barrier in mice. This breakthrough uses...
Gene Therapy Success in Hereditary Angioedema Patients
A group of patients with a hereditary disorder have had their lives transformed by a single treatment of a breakthrough gene-editing...
U.S. Gene Therapy Market Size, Share & Growth Report, 2033
According to Nova One Advisor, the U.S. gene therapy market size was valued at USD 3.19 billion in 2023 and...
10 gene therapy companies you should know about
The gene therapy sector is currently thriving within the biotech industry, particularly since the first CRISPR-based therapy was approved to...
Study Suggests Genetics as a Cause, Not Just a Risk, for Some Alzheimer’s
Scientists are proposing a new way of understanding the genetics of Alzheimer’s that would mean that up to a fifth...
