Gene therapy halts progression of rare genetic condition in young boy
Michael is checked by a nurse at SickKids before receiving gene therapy in a single-patient clinical trial for spastic paraplegia...
Michael is checked by a nurse at SickKids before receiving gene therapy in a single-patient clinical trial for spastic paraplegia...
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A novel gene therapy designed to target a form of inherited deafness restored hearing function in five children who were...
A UC San Francisco-led study has for the first time identified genetic variants that predict whether a patient is likely...
Children with hereditary deafness regained their hearing thanks to a type of gene therapy, a new study published on Wednesday...
Published: 11 October 2023Children born with hearing loss due to the genetic condition auditory neuropathy will be given a pioneering...
BlackfinBio has raised £2.75 million seed investment to advance revolutionary treatments for Hereditary Spastic Paraplegia (HSP). BlackfinBio has raised £2.75...
By Catherine Graham / Published Aug 10, 2023 Though almost every cell in your body contains a copy of each...