Gene therapy halts progression of rare genetic condition in young boy
Michael is checked by a nurse at SickKids before receiving gene therapy in a single-patient clinical trial for spastic paraplegia...
genetic
Gene Therapy Halts Progression of Young Boy’s Rare Genetic Condition
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New bilateral gene therapy shows promising results in treating genetic hearing loss
A novel gene therapy designed to target a form of inherited deafness restored hearing function in five children who were...
Genetic Discovery Reveals Who Can Benefit from Preterm Birth Therapy
A UC San Francisco-led study has for the first time identified genetic variants that predict whether a patient is likely...
Children with genetic deafness have hearing restored with gene therapy: Study
Children with hereditary deafness regained their hearing thanks to a type of gene therapy, a new study published on Wednesday...
World-first trial of gene therapy to cure children with rare type of genetic deafness begins
Published: 11 October 2023Children born with hearing loss due to the genetic condition auditory neuropathy will be given a pioneering...
University of Sheffield spinout company to pioneer novel therapies for genetic neurological diseases | News
BlackfinBio has raised £2.75 million seed investment to advance revolutionary treatments for Hereditary Spastic Paraplegia (HSP). BlackfinBio has raised £2.75...
Machine learning model could enable targeted gene therapies for genetic diseases
By Catherine Graham / Published Aug 10, 2023 Though almost every cell in your body contains a copy of each...
