New Gene Delivery Method Paves the Way for Advanced Brain Therapies
Gene therapies use genes to treat, prevent, or cure diseases and disorders. Small viruses called adeno-associated viruses (AAVs) are a...
method
Method that silences specific genes while leaving others unaffected could aid research and therapy
Fusion of translational repressors to dPspCas13b enhances translational repression efficacy. Credit: Nature Communications (2024). DOI: 10.1038/s41467-024-46412-7 RIKEN researchers have developed...
Scientists develop method to deliver larger genes to target cells
Gene therapy currently represents the most promising approach for the treatment of hereditary diseases. Yet despite significant breakthroughs in recent...
