New Gene Delivery Method Paves the Way for Advanced Brain Therapies
Gene therapies use genes to treat, prevent, or cure diseases and disorders. Small viruses called adeno-associated viruses (AAVs) are a...
Gene therapies use genes to treat, prevent, or cure diseases and disorders. Small viruses called adeno-associated viruses (AAVs) are a...
Fusion of translational repressors to dPspCas13b enhances translational repression efficacy. Credit: Nature Communications (2024). DOI: 10.1038/s41467-024-46412-7 RIKEN researchers have developed...
Gene therapy currently represents the most promising approach for the treatment of hereditary diseases. Yet despite significant breakthroughs in recent...