Unlocking the Potential of Gene Therapy for Genetic Skin Disorders
Original story from the University of British Columbia (British Columbia, Canada). Gene-editing tools like CRISPR have unlocked new treatments for...
Genetics and Gene Therapy Research
Gene therapy for blindness and vision loss gains momentum
Since the approval of the first-ever gene therapy for blindness, there has been a wave of biotechs developing gene therapy...
Next-generation gene therapy tools built by UH scientist
Reading time: 2 minutesAssistant Professor Jesse Owens using a program to model the structure of his integrase protein. What if,...
UMass Chan licenses gene therapy for rare genetic disorder to Raiden Science Foundation
Raiden Pham, who was diagnosed with UBA5 disorder in 2021, with his mother Linda Pham. Photo courtesy of Tommy and Linda...
Opus Genetics Launches Gene Therapy Clinical Trial for MERTK-related Retinitis Pigmentosa
Opus Genetics, Inc. The trial is funded through Abu Dhabi’s Healthcare Research and Innovation Fund Clinical development activities will commence...
Single protein is key to treating a deadly genetic heart disease targeting young athletes
A research team at the University of California San Diego has discovered a novel and promising method of treating arrhythmogenic...
Opus Genetics starts MERTK RP gene therapy trial
Opus Genetics (Nasdaq: IRD) launched a clinical trial for OPGx-MERTK, an AAV-based gene therapy for...
Opus Genetics Launches Gene Therapy Clinical Trial for
The trial is funded through Abu Dhabi’s Healthcare Research and Innovation FundClinical development activities will commence at Cleveland Clinic Abu...
Scientists just made gene editing far more powerful
Some inherited diseases, including cystic fibrosis, hemophilia, and Tay Sachs disease, involve multiple genetic mutations within a person's DNA. Even...
