HiFi sequencing delivers confidence for cell and gene therapy research
The emerging fields of cell and gene therapy hint at a future with treatments and cures for diseases that,...
The emerging fields of cell and gene therapy hint at a future with treatments and cures for diseases that,...
Summary: A new gene therapy has restored vision in patients with Leber congenital amaurosis type I (LCA1), a rare genetic...
Graphical abstract. Credit: Nucleic Acids Research (2024). DOI: 10.1093/nar/gkae534 For decades, scientists have dreamed of a future where genetic diseases,...
While viral vector-based gene therapies, such as those employing adeno-associated viruses, are increasing in popularity, scientists face several challenges when...
Gene therapy has captured the imagination of scientists and science fiction fans alike. But as its development gains momentum, scientists...
Columbia researchers discovered that bacteria can create free-floating, temporary genes outside their chromosomes, challenging the long-held belief that all genetic...
Columbia researchers discovered that bacteria can create free-floating, temporary genes outside their chromosomes, challenging the long-held belief that all genetic...
Gene therapy could potentially cure genetic diseases but it remains a challenge to package and deliver new genes to specific...
Robin Alderman faces an agonizing reality: Gene therapy might cure her son Camden’s rare, inherited immune deficiency. But it’s not...