A bespoke gene-editing treatment for a baby born with a life-threatening disorder : Shots
KJ Muldoon, who was born at Children's Hospital of Philadelphia in August, reaches out to doctors after being treated for...
Born
Baby born deaf can hear after breakthrough gene therapy
Opal Sandy from Oxfordshire is the first patient treated in a global gene therapy trial, which shows 'mind-blowing' results. She...
Experimental Gene Therapy Enables Hearing in Five Children Born Deaf
At a glance:Trial treated six children aged 1 to 7 who had a mutation in the OTOF gene, which manufactures...
