REGN Reports Encouraging Data on Gene Therapy for Genetic Hearing Loss
Regeneron Pharmaceuticals, Inc. REGN announced updated data on its investigational gene therapy DB-OTO from the CHORD study.This gene therapy is...
gene
Opus Genetics reports positive pediatric data from LCA5 gene therapy study
Opus Genetics, Inc. released positive data from a pediatric cohort in an ongoing phase 1/2 clinical study evaluating OPGx-LCA5, an...
New gene therapy strategy reactivates dormant genes to treat blood disorders
Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them closer to...
New gene therapy for Huntington’s ‘changes everything’, say researchers
UK researchers say they have slowed the progression of the fatal neural condition Huntington's disease for the first time with...
AI-powered CRISPR could lead to faster gene therapies, Stanford Medicine study finds
Yilong Zhou, a visiting undergraduate student from Tsinghua University, used CRISPR-GPT to successfully active genes in A375 melanoma cancer cells...
Researchers Advance Gene Therapy for CLIC5-Related Inner Ear Dysfunction
Summary: Researchers at Tel Aviv University and collaborators have developed a novel gene therapy using an optimized viral vector that...
Breakthrough gene therapy could one day cure genetic hearing loss
Tel Aviv , September 15 (ANI/TPS): Israeli and US scientists have developed a promising new gene therapy that could one...
New gene therapy is life changing for teenage patient | UCL News
A teenager with a rare, life-limiting genetic condition is off to university after receiving a pioneering gene therapy developed by...
Gene that human ancestors lost millions of years ago could help treat gout
Millions of years ago, humans' ancestors lost the function of a specific gene — but switching that gene back on...
