Gene circuits enable more precise control of gene therapy | MIT News
Many diseases are caused by a missing or defective copy of a single gene. For decades, scientists have been working...
gene
Single Dose Gene Therapy Market Size, Report by 2034
Single-Dose Gene Therapy Market Size and Forecast 2025 to 2034 Single-dose gene therapy market sees rapid growth driven by advancements...
Breakthrough gene therapy reverses genetic deafness across age groups
Using gene therapy to treat hereditary deafness is safe and effective in both children and adults, according to new findings...
Gene therapy trial offers breakthrough for rare genetic disorder
Credit: Pixabay/CC0 Public Domain A study evaluating a pioneering lentivirus (LV)-mediated gene therapy trial for classical Fabry disease showed promising...
The Latest Advances in Cell and Gene Therapy
The Current State of CGTsBreakthrough Technologies Manufacturing Hurdles in CGT DevelopmentFuture Outlook Cell and gene therapies (CGTs) represent the cutting edge...
New era of gene therapy treats baby with ultrarare disease
Dr Kiran Musunuru and Dr Rebecca Ahrens-Nicklas with patient KJ. Credit: Children’s Hospital of Philadelphia In a major step forward...
In a first, congenital deafness in teens and adults treated with new gene therapy
Up to 3 in every 1,000 newborns has hearing loss in one or both ears. While cochlear implants offer remarkable...
Scientists discover new approach to gene therapy
Credit: bioRxiv (2025). DOI: 10.1101/2025.01.13.632719 Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes...
Gene Therapy Can Restore Hearing in Adults, First-of-Its-Kind Trial Shows : ScienceAlert
Up to three in every 1,000 newborns has hearing loss in one or both ears. While cochlear implants offer remarkable...
