Gene therapy hailed as ‘medical magic wand’ for hereditary swelling disorder | Medical research
A groundbreaking gene therapy has been hailed as a “medical magic wand” after the treatment transformed the lives of patients...
Hereditary
Gene Therapy Success in Hereditary Angioedema Patients
A group of patients with a hereditary disorder have had their lives transformed by a single treatment of a breakthrough gene-editing...
Hereditary spastic paraplegia: Journey to a treatment
Darius Ebrahimi-Fakhari, MD, PhD (Photo: Michael Goderre, Boston Children's Hospital) In 2016, Darius Ebrahimi-Fakhari, MD, PhD, a neurology fellow at...
