UMass Chan licenses gene therapy for rare genetic disorder to Raiden Science Foundation
Raiden Pham, who was diagnosed with UBA5 disorder in 2021, with his mother Linda Pham. Photo courtesy of Tommy and Linda...
UMass
Gene therapy developed for maple syrup urine disease shows promise, new UMass Chan study reports
A study led by UMass Chan Medical School researchers demonstrated that a gene therapy to correct a mutation that causes...
UMass Researchers Advance Gene Therapy for MSUD
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Family with child affected by SPG4 visits UMass Chan researchers developing gene therapy
Jack Laidlaw, 7, of Ottawa, Ontario, visited UMass Chan with his family to meet researchers working on a gene therapy...
