New hope for children with devastating rare genetic disorder, thanks to world-first research in Manchester
The parents of a three-year-old boy born with a devastating, life-limiting genetic condition say they are now excited for his...
Worldfirst
World-first CRISPR therapy could ‘transform’ treatment for rare genetic diseases, but key challenges lie ahead
It has been described as a revolutionary technology — and won its inventors a Nobel Prize.CRISPR gene editing, often simply...
World-first trial of gene therapy to cure children with rare type of genetic deafness begins
Published: 11 October 2023Children born with hearing loss due to the genetic condition auditory neuropathy will be given a pioneering...
